FDA Approves First Gene Therapy for Young Children with Sickle Cell Disease
First publishedJul 1, 21:29 UTC
Last updatedJul 12, 12:32 UTC · 13m ago
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The report
The U.S. Food and Drug Administration today issued a supplemental approval for Casgevy (exagamglogene autotemcel) for patients aged 2 years and older with either sickle cell disease (SCD) with recurrent vaso-occlusive crises (VOCs) or transfusion-dependent β thalassemia (TDT).
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organizationCasgevyorganizationDrug AdministrationorganizationFDA Approves First GeneorganizationSCDorganizationSickle Cell Disease. TheorganizationTherapyorganizationVOCsorganizationYoung Children
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