#Rare Disease
Latest news articles tagged with "Rare Disease". Follow the timeline of events, related topics, and entities.
Articles (2)
-
🇺🇸 They're in a race to save their children with a rare disease. A newly approved drug has given them hope.
[USA]
After a string of denials for rare disease treatments, the FDA greenlit a drug for Hunter syndrome, a progressive illness affecting about 500 Americans.
Related: #Medical Hope -
🇺🇸 FDA approves leucovorin as first drug for rare genetic disorder, after touting it as autism treatment
[USA]
The move comes months after the Trump administration touted leucovorin as a potential therapy for a broader group of patients with autism symptoms.
Related: #FDA Approval, #Drug Repurposing
Key Entities (1)
- Food and Drug Administration (1 news)
About the topic: Rare Disease
The topic "Rare Disease" aggregates 2+ news articles from various countries.