🌐 Entity
Alexander disease
Rare genetic disorder of the white matter of the brain
📊 Rating
1 news mentions · 👍 0 likes · 👎 0 dislikes
📌 Topics
- Regulatory Approval (1)
- Rare Disease Treatment (1)
🏷️ Keywords
FDA (1) · zilganersen (1) · Alexander disease (1) · neurological disorder (1) · treatment application (1) · regulatory review (1) · rare disease (1)
📖 Key Information
Alexander disease is a very rare autosomal dominant leukodystrophy, which are neurological conditions caused by anomalies in the myelin which protects nerve fibers in the brain. The most common type is the infantile form that usually begins during the first two years of life. Symptoms include mental and physical developmental delays, followed by the loss of developmental milestones, an abnormal increase in head size and seizures.
📰 Related News (1)
🔗 Entity Intersection Graph
People and organizations frequently mentioned alongside Alexander disease:
-
Food and Drug Administration · 1 shared articles